Status:

COMPLETED

An Extension Study to Determine the Efficacy and Safety of STI571 in Participants With Chronic Myeloid Leukemia Who Are Refractory to or Intolerant of Interferon-Alpha

Lead Sponsor:

Novartis Pharmaceuticals

Conditions:

Leukemia, Myelogenous, Chronic, BCR-ABL Positive

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

During the Core Phase of the study, participants received STI571 at a dose of 400 milligrams (mg) daily for up to 12 months. Participants completing 12 months of therapy were eligible to continue trea...

Eligibility Criteria

Inclusion

  • Participants included in the study were:
  • Consenting males or females greater than or equal to (≥)18 years of age with Philadelphia chromosome positive (Ph+) chronic myeloid leukemia (CML).
  • With a documented failure of interferon-alpha (IFN) or an IFN-containing therapy, characterized as resistance or refractoriness defined as any of the following:
  • Hematologic Resistance - Failure to achieve a complete hematological response (CHR), lasting for at least 1 month despite 6 or more months of IFN or an IFN-containing regimen, in which IFN was administered at a dose of at least 25 million international units (MIU) per week. During this treatment period the cumulative duration of hydroxyurea therapy may not have exceeded 50% of the treatment period with the IFN-containing regimen.
  • Cytogenetic Resistance - Bone marrow cytogenetics showing ≥65% Ph+ after one year of IFN-based therapy,
  • Cytogenetic Refractoriness - An increase in the Ph+ chromosome in BM cells by at least 30 percentage points (e.g. from 20% to 50%, or from 30% to 60%) confirmed by two samples at least 1 month apart, or an absolute increase to ≥65%,
  • Hematologic Refractoriness - A rising white blood cell count (WBC) \[to a level ≥20 x 10\^9/L confirmed by two samples taken at least two weeks apart\] for participants achieving a complete hematologic response while receiving IFN or an IFN-containing regimen. This regimen must have included IFN at a dose of at least 25 MIU administered per week. During this treatment period the cumulative duration of hydroxyurea therapy may not have exceeded 50% of the treatment period with the IFN-containing regimen.
  • In this report all refractory populations were referred to as "relapsed" populations.
  • With a documented intolerance to IFN therapy defined as a ≥Grade 3 non-hematologic toxicity persisting for at least one month, for participants receiving IFN or an IFN- containing regimen. IFN was to be administered at a dose of at least 25 MIU/week. Participants who were intolerant of IFN were to have been diagnosed ≥6 months prior to the time of entry into the study.

Exclusion

  • Participants excluded from the study were:
  • Females of childbearing potential without a negative pregnancy test prior to the initiation of study drug. Barrier contraceptive precautions were to be used throughout the trial in both sexes.
  • With serum bilirubin and creatinine concentrations more than twice the upper limit of the normal range (ULN).
  • With serum glutamic oxaloacetic transaminase (SGOT) and serum glutamic pyruvic transaminase (SGPT) more than twice the ULN.
  • With \>15% of blasts or basophils in peripheral blood (PB) or bone marrow (BM).
  • With ≥30% of blasts plus promyelocytes in PB or BM.
  • With a platelet count of less than (\<)100 x 10\^9/L.
  • With an Eastern Cooperative Oncology Group (ECOG) Performance Status Score ≥3.
  • Receiving busulfan within 6 weeks of Day 1.
  • Receiving treatment with IFN or cytosine arabinoside (Ara-C) within 14 days of Day 1.
  • Receiving treatment with hydroxyurea within 7 days of Day 1.
  • Receiving other investigational agents within 28 days of Day 1.
  • With prior marrow or stem cell transplantation.

Key Trial Info

Start Date :

December 6 1999

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

November 29 2013

Estimated Enrollment :

532 Patients enrolled

Trial Details

Trial ID

NCT00171223

Start Date

December 6 1999

End Date

November 29 2013

Last Update

July 22 2021

Active Locations (28)

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Page 1 of 7 (28 locations)

1

UCLA Medical Center

Los Angeles, California, United States, 90095

2

H. Lee Moffet Cancer Center & Research Institute/Univ of South Florida

Tampa, Florida, United States, 33612

3

Northwestern Univ meical School/Robert H. Lurie Comprehensive Cancer Center

Chicago, Illinois, United States, 60611

4

Johns Hopkins Oncology Center

Baltimore, Maryland, United States, 21231