Status:

COMPLETED

Bortezomib in Treating Patients With Myelodysplastic Syndromes

Lead Sponsor:

University of Rochester

Conditions:

Myelodysplastic Syndromes

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

RATIONALE: Bortezomib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. PURPOSE: This phase II trial is studying how well bortezomib works in treating patien...

Detailed Description

OBJECTIVES: Primary * Determine the efficacy of bortezomib, in terms of reduced cytopenia, in patients with myelodysplastic syndromes. * Determine the safety and toxic effects of this drug in these ...

Eligibility Criteria

Inclusion

  • DISEASE CHARACTERISTICS:
  • Diagnosis of myelodysplastic syndromes (MDS)
  • Requires treatment or transfusion support for MDS, as indicated by 1 of the following:
  • Demonstrates transfusion or epoetin alfa dependence
  • Transfusion dependence is defined as requiring ≥ 2 units of packed RBCs within an 8-week period prior to study entry
  • Hemoglobin \< 11g/dL on 2 separate occasions 2 weeks apart
  • No iron, cyanocobalamin (vitamin B\_12), or folic acid deficiency or other causes of anemia
  • Must have 1 of the following FAB subtypes:
  • Refractory anemia
  • Refractory anemia with ringed sideroblasts
  • Refractory anemia with excess blasts
  • Secondary MDS (if ≥ 3 years since active primary cancer)
  • No chronic myelomonocytic leukemia
  • Not refractory to platelet transfusion support (i.e., inability to maintain platelet count \> 20,000/mm\^3 with transfusion)
  • No current acute myelogenous leukemia (e.g., \> 30% blasts)
  • PATIENT CHARACTERISTICS:
  • Performance status
  • Karnofsky 50-100%
  • Life expectancy
  • At least 6 months
  • Hematopoietic
  • See Disease Characteristics
  • Hepatic
  • Bilirubin ≤ 2 mg/dL
  • AST and ALT \< 2 times upper limit of normal
  • Renal
  • Creatinine clearance ≥ 30 mL/min
  • Cardiovascular
  • No significant cardiovascular condition that would preclude study participation
  • No uncontrolled hypertension
  • Pulmonary
  • No significant pulmonary condition that would preclude study participation
  • Immunologic
  • No serious concurrent infection
  • Active infections must be adequately treated with antibiotics prior to study entry
  • No hypersensitivity to bortezomib, boron, or mannitol
  • Other
  • Not pregnant or nursing
  • Negative pregnancy test
  • Fertile patients must use effective contraception during and for up to 4 weeks after completion of study treatment
  • No peripheral neuropathy ≥ grade 2
  • No uncontrolled seizure activity, as defined by no activity within the past year on stable anticonvulsant medications
  • No other malignancy within the past 3 years except adequately treated basal cell skin cancer or carcinoma in situ of the cervix
  • No endocrine, neurologic, or other systemic disease that would preclude study entry
  • PRIOR CONCURRENT THERAPY:
  • Biologic therapy
  • See Disease Characteristics
  • No prior allogeneic bone marrow transplantation
  • Concurrent transfusion support allowed
  • Concurrent epoetin alfa or darbepoetin alfa allowed if initiated before start of study therapy, dose is stable for ≥ 4 weeks, and dose is stable during study participation
  • No concurrent platelet growth factor support
  • No concurrent thalidomide
  • Chemotherapy
  • No concurrent chemotherapy
  • No concurrent hydroxyurea
  • Endocrine therapy
  • Concurrent corticosteroids for chronic autoimmune or inflammatory condition allowed if initiated before start of study therapy and maintained on a stable or decreasing dose
  • Other
  • Recovered from all prior therapies
  • At least 4 weeks since prior MDS therapy, except epoetin alfa, darbepoetin alfa, filgrastim (G-CSF), pegfilgrastim (G-CSF), or transfusion support
  • At least 30 days since prior investigational agents
  • No prior bortezomib
  • No other concurrent investigational agents
  • No other concurrent therapy for MDS

Exclusion

    Key Trial Info

    Start Date :

    May 1 2005

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ACTUAL

    End Date :

    October 1 2010

    Estimated Enrollment :

    8 Patients enrolled

    Trial Details

    Trial ID

    NCT00262873

    Start Date

    May 1 2005

    End Date

    October 1 2010

    Last Update

    May 9 2016

    Active Locations (1)

    Enter a location and click search to find clinical trials sorted by distance.

    Page 1 of 1 (1 locations)

    1

    James P. Wilmot Cancer Center at University of Rochester Medical Center

    Rochester, New York, United States, 14642