Status:
COMPLETED
Long-term Lung Function and Disease Progression in Children With Early Onset Primary Ciliary Dyskinesia Lung Disease
Lead Sponsor:
University of North Carolina, Chapel Hill
Collaborating Sponsors:
National Heart, Lung, and Blood Institute (NHLBI)
Conditions:
Kartagener Syndrome
Eligibility:
All Genders
Up to 4 years
Brief Summary
Primary ciliary dyskinesia (PCD), also known as Kartagener syndrome, is a genetic disorder of the cilia, which are microscopic hair-like cells. Cilia work to keep the respiratory system clean by movin...
Detailed Description
PCD, or Kartagener syndrome, is a genetic disorder that causes hair-like cells called cilia to move improperly, or in some cases, not at all. Cilia are needed to help clear the respiratory system of p...
Eligibility Criteria
Inclusion
- Younger than 5 years of age
- Diagnosis of PCD or probable PCD based on criteria listed above
- Parent or legal guardian willing to give informed consent
Exclusion
- Unable to attend follow-up appointments
- History of lung transplant
- Any co-existing severe diseases that may have significant impact on lung function, respiratory infections, or overall health status (i.e., severe congenital heart disease, severe scoliosis, AIDS, cancer, or end-stage kidney disease)
Key Trial Info
Start Date :
July 1 2008
Trial Type :
OBSERVATIONAL
Allocation :
ACTUAL
End Date :
August 1 2019
Estimated Enrollment :
48 Patients enrolled
Trial Details
Trial ID
NCT00722878
Start Date
July 1 2008
End Date
August 1 2019
Last Update
October 7 2019
Active Locations (6)
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1
Stanford University, Palo Alto
Palo Alto, California, United States, 94304
2
The Children's Hospital, Denver
Denver, Colorado, United States, 80045
3
Washington University in St. Louis
St Louis, Missouri, United States, 63110
4
University of North Carolina, Chapel Hill
Chapel Hill, North Carolina, United States, 27599