Status:

COMPLETED

Clinical Trial of Aplidin® in Patients With Primary Myelofibrosis

Lead Sponsor:

PharmaMar

Conditions:

Myelofibrosis

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This is an open-label, Phase II Clinical Trial of Aplidin® (plitidepsin) in Patients with Primary Myelofibrosis and post polycythemia vera/essential thrombocythemia (Post-PV/ET) Myelofibrosis.

Detailed Description

This trial tries to assess response rate (ORR) of plitidepsin in patients with: primary myelofibrosis (PMF), post-polycythemia vera myelofibrosis (post-PV MF), or post-essential thrombocythemia myelo...

Eligibility Criteria

Inclusion

  • Diagnosis of Primary Myelofibrosis (PMF) or Post Polycythemia Vera/Essential Thrombocythemia Myelofibrosis(post-ET/PV MF) as per revised World Health Organization (WHO) criteria.
  • High-risk or intermediate-2 risk Myelofibrosis (MF) as defined by the International Prognostic Scoring System (IPSS); or intermediate-I risk MF associated with symptomatic splenomegaly/hepatomegaly and/or unresponsive to available therapy.
  • At least 18 years of age, with life expectancy of ≥12 weeks.
  • Able to provide informed consent and being willing to sign an informed consent form (ICF).
  • Eastern Cooperative Oncology Group (ECOG) performance status ≤2.
  • Evidence of acceptable organ function within seven days of initiating study drug

Exclusion

  • Previous treatment with plitidepsin.
  • Any of the following therapies within two weeks prior to initiation of study drug:
  • chemotherapy (e.g., hydroxyurea),
  • immunomodulatory drug therapy (e.g., thalidomide),
  • immunosuppressive therapy,
  • corticosteroids \>10 mg/day prednisone or equivalent, or
  • erythropoietin.
  • Incomplete recovery from major surgery within four weeks of study entry.
  • Radiation therapy within four weeks of study entry.
  • Women of childbearing potential
  • Women who are pregnant or are currently breastfeeding.
  • Myopathy grade \> 2
  • Known positive status for human immunodeficiency virus (HIV).
  • Active hepatitis B or C virus (HBV or HCV) infection
  • Diagnosis of another invasive malignancy
  • Any acute active infection.
  • Known hypersensitivity to the study drug or any of its formulation components (e.g., Cremophor®).
  • Treatment with any investigational product in the 30 days before inclusion in the study.

Key Trial Info

Start Date :

July 1 2010

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 1 2011

Estimated Enrollment :

12 Patients enrolled

Trial Details

Trial ID

NCT01149681

Start Date

July 1 2010

End Date

February 1 2011

Last Update

October 12 2020

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Mayo Clinic

Rochester, Minnesota, United States, 55905

2

Azienda Ospedaliero Universitaria Careggi di Firenze

Florence, Italy, 50134