Status:
NO_LONGER_AVAILABLE
Dichloroacetate Treatment of Congenital Lactic Acidosis Phase B: Expanded Access
Lead Sponsor:
University of Florida
Conditions:
Mitochondrial Enzyme Deficiencies
Eligibility:
FEMALE
18-50 years
Brief Summary
Expanded access to DCA as continued treatment for congenital lactic acidosis.
Detailed Description
Subjects who participated in a Phase 3 Randomized Controlled Trial of DCA for treatment of Congenital Lactic Acidosis (CLA) are eligible to continue treatment with investigational medication DCA at th...
Eligibility Criteria
Inclusion
- Diagnosis of congenital lactic acidosis
- Participation in Study: #183-1992: Dichloroacetate Treatment of Congenital Lactic Acidosis
Exclusion
- Intolerance to DCA
Key Trial Info
Start Date :
Trial Type :
EXPANDED_ACCESS
End Date :
Estimated Enrollment :
Patients enrolled
Trial Details
Trial ID
NCT01797276
Last Update
August 8 2017
Active Locations (1)
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1
University of Florida Box 100226
Gainesville, Florida, United States, 32610-0226