Status:
COMPLETED
Palliative Care in Spinal Muscular Atrophy (SMA) 1
Lead Sponsor:
Assistance Publique - Hôpitaux de Paris
Collaborating Sponsors:
URC-CIC Paris Descartes Necker Cochin
Conditions:
Spinal Muscular Atrophy 1
Eligibility:
All Genders
1-1 years
Phase:
NA
Brief Summary
The purpose of this study is to evaluate the quality of supportive and palliative care for SMA type 1 patients.
Detailed Description
Spinal Muscular Atrophy Type I (SMA I) is the most severe form of SMA. It presents in infancy and death occurs by 2 years. There is actually no curative treatment for this pathology. Support and help ...
Eligibility Criteria
Inclusion
- SMA type 1 under 1 an
- Genetic confirmation
Exclusion
- No genetic confirmation
- SMA type 1 over 1 year
Key Trial Info
Start Date :
June 1 2012
Trial Type :
INTERVENTIONAL
Allocation :
ACTUAL
End Date :
June 11 2018
Estimated Enrollment :
39 Patients enrolled
Trial Details
Trial ID
NCT01862042
Start Date
June 1 2012
End Date
June 11 2018
Last Update
September 11 2025
Active Locations (1)
Enter a location and click search to find clinical trials sorted by distance.
1
Necker Hospital
Paris, France, 75015