Status:

TERMINATED

A Phase 2A Study of ALXN1007 in Participants With Newly Diagnosed Acute Lower Gastrointestinal Graft-Versus-Host Disease

Lead Sponsor:

Alexion Pharmaceuticals, Inc.

Conditions:

Acute Graft-Versus-Host Disease

GIGVHD

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

The objectives of this trial were to evaluate the safety, tolerability, pharmacokinetics/pharmacodynamics (PK/PD) and efficacy of intravenous (IV) ALXN1007 in participants with acute graft-versus-host...

Detailed Description

This was a Phase 2A open-label, non-randomized study to evaluate the safety, tolerability, PK/PD, and efficacy of ALXN1007 (a C5a inhibitor) in up to 36 participants with newly diagnosed acute GVHD of...

Eligibility Criteria

Inclusion

  • Participants must be males or females age 18 years or older.
  • Participants with Stage 1 to 4 (per the Modified Keystone Grading Schema) acute GVHD of the lower GI tract, without signs of chronic GVHD, at the time of diagnosis, which developed in the first 180 days following allogeneic hematopoietic cell transplantation (HCT) using bone marrow, peripheral blood, or cord blood; or after preplanned donor lymphocyte infusion.
  • Participants are willing to undergo or must have had an endoscopy of the upper and/or lower GI tract and biopsy to confirm GI GVHD.
  • Participants must be receiving systemic corticosteroids.
  • Participants with an absolute neutrophil count (ANC) \>500/microliter (μL) at Screening.
  • Participants and spouse/partner who are of childbearing potential must be using high effective contraception consisting of 2 forms of birth control (at least 1 of which much be barrier method) starting at Screening and continuing through the entire study (for at least 3 months after the last dose of ALXN1007 if study treatment is stopped early or participant withdraws consent).
  • Male participants must not donate sperm during the Screening and Treatment periods, and for at least 3 months after the last dose of ALXN1007.
  • Stage of acute GVHD of the lower GI tract will be determined using the Modified Keystone Grading Schema.

Exclusion

  • Participants with a body weight \> 140 kg (for Cohorts dosing 20 mg/kg of ALXN1007 and higher only).
  • Participants with signs and symptoms of chronic GVHD.
  • Participants with an active uncontrolled infection.
  • Participants who test positive for Clostridium difficile (C. difficile) at Screening.
  • Participants with relapsed/persistent malignancy requiring rapid immune suppression withdrawal.
  • Participants who received an unplanned (not part of the original transplant therapy plan) donor lymphocyte infusion.
  • Participants who received previous systemic treatment for acute GVHD, except for a maximum of 3 days (72 hours) of 2 mg/kg corticosteroid therapy.
  • Participants with unresolved veno-occlusive disease of the liver.
  • Participants with creatinine clearance \<40 milliliters (mL)/minute at Screening, as calculated by the Cockcroft-Gault formula.
  • Participants known to be infected with human immunodeficiency virus (HIV), hepatitis B, or hepatitis C.
  • Participants known to have an uncontrolled thyroid disorder.
  • Participants who are pregnant, breast feeding, or sexually active and unwilling to use effective birth control for the duration of the study.
  • Participants who participated in any other investigational drug trial or had exposure to any other investigational agent, device, or procedure \<4 weeks prior to Screening and throughout the entire trial, with the exception of investigational drugs administered prophylactically for cytomegalovirus (CMV) post allogeneic HCT.

Key Trial Info

Start Date :

November 14 2014

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 27 2017

Estimated Enrollment :

25 Patients enrolled

Trial Details

Trial ID

NCT02245412

Start Date

November 14 2014

End Date

February 27 2017

Last Update

January 3 2019

Active Locations (12)

Enter a location and click search to find clinical trials sorted by distance.

Page 1 of 3 (12 locations)

1

City of Hope

Duarte, California, United States, 91010

2

Emory University Hospital

Atlanta, Georgia, United States, 30322

3

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States, 48201

4

University of Minnesota Medicine - Hematology, Oncology and Transplantation Office

Minneapolis, Minnesota, United States, 55455