Status:

COMPLETED

Survey on Cardiovascular Events in Patients With Metabolic Disease on Chronic Carnitine Supplementation

Lead Sponsor:

University of South Florida

Collaborating Sponsors:

National Institutes of Health (NIH)

Conditions:

Metabolic Disorders

Eligibility:

All Genders

Brief Summary

The purpose of this study is to learn about the effects of long term carnitine use in patients with metabolic disorders and its potential relationship to cardiovascular events.

Detailed Description

This online cross-sectional survey will examine the self-reported long-term carnitine use in patients with metabolic disorders and any potential relationship to cardiovascular events.

Eligibility Criteria

Inclusion

  • Diagnosis of mitochondrial disease or any other metabolic disorder
  • Any age group
  • NAMDC or RDCRN registry participant

Exclusion

  • Inability to provide informed consent and complete survey
  • Lack of participation in NAMDC or RDCRN registry

Key Trial Info

Start Date :

September 1 2014

Trial Type :

OBSERVATIONAL

Allocation :

ACTUAL

End Date :

June 1 2016

Estimated Enrollment :

106 Patients enrolled

Trial Details

Trial ID

NCT02311270

Start Date

September 1 2014

End Date

June 1 2016

Last Update

September 23 2016

Active Locations (1)

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1

University of South Florida

Tampa, Florida, United States, 33612