Status:

RECRUITING

Nintedanib in Patients With Bronchiolitis Obliterans Syndrome Following Hematopoietic Stem Cell Transplantation

Lead Sponsor:

University Hospital, Basel, Switzerland

Conditions:

Bronchiolitis Obliterans Syndrome (BOS)

Bronchiolitis Obliterans (BO)

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This study investigates the safety and tolerability of Nintedanib in patients with bronchiolitis obliterans syndrome (BOS) following allogeneic hematopoietic cell transplantation. All study patients w...

Detailed Description

Allogeneic hematopoietic stem cell transplantation (HCT) is an established treatment option for several malignant and non-malignant disorders. An important limitation of long-term survival after HCT i...

Eligibility Criteria

Inclusion

  • Inclusion Criteria:
  • Time interval from transplant \</= 5 years at the time of inclusion
  • BOS as defined per the National Institute of Health (NIH) criteria:
  • FEV1/vital capacity \< 0.7 or the fifth percentile of predicted.
  • FEV1 \< 75% of predicted with ≥ 10% decline over less than 2 years.
  • Absence of infection in the respiratory tract, documented with investigations directed by clinical symptoms, such as chest radiographs, computed tomographic (CT) scans, or microbiologic cultures (sinus aspiration, upper respiratory tract viral screen, sputum culture, and broncho-alveolar lavage).
  • One of the 2 supporting features of BOS: 1. Evidence of air trapping by expiratory CT or small airway thickening or bronchiectasis by high-resolution chest CT, or 2. Evidence of air trapping by PFTs: residual volume \> 120% of predicted or residual volume/total lung capacity elevated outside the 90% confidence interval and prior or current diagnosis of cGvHD per NIH criteria or histologically proven BO
  • Diagnosis of BOS within 6 months before enrollment or prior diagnosis of BOS with an absolute decline of the percentage of predicted forced expiratory volume in 1 second (FEV1) by \>/= 10% within the past 12 months before inclusion
  • Exclusion Criteria
  • Known intolerance to Nintedanib or any of its component
  • Pregnancy or nursing
  • Serum ALT \> 5 x upper limit of normal (ULN) unless explained entirely by liver GvHD or total bilirubin \> 3x ULN unless explained entirely by liver GvHD
  • Any acute pulmonary infection with viruses, bacteria or fungi within four weeks before study inclusion
  • Chronic oxygen therapy; non-invasive ventilation
  • Inability to give informed consent or to perform repeated pulmonary function tests (PFT)
  • Life expectancy \< 1 year at the time of enrolment as suggested by the treating physician
  • Hematologic malignancy in hematologic relapse
  • Symptomatic angina pectoris
  • Therapeutic anticoagulation (primary or secondary prophylactic platelet anti-aggregation allowed)
  • Recent abdominal surgery or untreated gastric ulcer

Exclusion

    Key Trial Info

    Start Date :

    March 20 2019

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ESTIMATED

    End Date :

    December 1 2026

    Estimated Enrollment :

    20 Patients enrolled

    Trial Details

    Trial ID

    NCT03805477

    Start Date

    March 20 2019

    End Date

    December 1 2026

    Last Update

    December 15 2025

    Active Locations (3)

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    Page 1 of 1 (3 locations)

    1

    King Faisal Specialist Hospital & Research Centre

    Riyadh, Saudi Arabia, 11471

    2

    Clinic of Hematology, University Hospital Basel

    Basel, Switzerland, 4031

    3

    Clinic of Respiratory Medicine, University Hospital Basel

    Basel, Switzerland, 4031