Status:

RECRUITING

Treatment of Hemophilia A Patients With FVIII Inhibitors

Lead Sponsor:

Emory University

Collaborating Sponsors:

Octapharma

Conditions:

Hemophilia A

Eligibility:

MALE

Brief Summary

This is a non-interventional, multicenter, observational, international study in male persons with haemophilia A who have developed inhibitors to any replacement coagulation factor VIII (FVIII) produc...

Detailed Description

This study will capture different approaches in the management of persons with haemophilia A (HA) and inhibitors. HA is a serious blood coagulation disorder caused by a deficiency in FVIII that result...

Eligibility Criteria

Inclusion

  • Male persons with haemophilia A, of any severity, who have a historical inhibitor titer ≥ 0.6 BU/mL, including those who have failed previous immune tolerance induction (ITI) attempt(s)
  • Persons undergoing ITI with Nuwiq, octanate, or wilateor undergoing ITI with Nuwiq®, octanate® or wilate® and receiving prophylactic therapy with emicizumab, activated prothrombin complex concentrate (aPCC), or activated recombinant factor VII (rFVIIa)
  • Participants or participants' parent(s)/legal guardian(s) must be capable of giving signed informed consent and be able to understand the trial documents

Exclusion

  • Participants are excluded from the trial if any coagulation disorder other than haemophilia A is diagnosed
  • Partly retrospective patients will be excluded if detailed documentation on treatment, all bleeding episodes, inhibitor titers, and FVIII levels is not available for the retrospective period

Key Trial Info

Start Date :

March 17 2020

Trial Type :

OBSERVATIONAL

Allocation :

ESTIMATED

End Date :

June 1 2029

Estimated Enrollment :

120 Patients enrolled

Trial Details

Trial ID

NCT04023019

Start Date

March 17 2020

End Date

June 1 2029

Last Update

September 5 2025

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Arthur M. Blank Hospital

Atlanta, Georgia, United States, 30329

2

HZRM Hämophilie-Zentrum Rhein Main

Mörfelden-Walldorf, Germany, 64546