Status:

COMPLETED

Clinical Outcomes of Triple Combination Therapy in Severe Cystic Fibrosis Disease.

Lead Sponsor:

National Jewish Health

Conditions:

Cystic Fibrosis

Eligibility:

All Genders

12+ years

Brief Summary

This is an observational study of people with severe cystic fibrosis that are eligible for Vertex's triple combination therapy through its expanded access. Pulmonary health, intestinal health, and the...

Eligibility Criteria

Inclusion

  • Confirmed diagnosis of Cystic Fibrosis
  • Ability to reproducibly perform spirometry (according to ATS criteria)
  • Physician decision to treat with TCT through the EAP program
  • Ability to understand and sign a written informed consent or assent and comply with the requirements of the study

Exclusion

  • History of hypersensitivity to VX 445, VX 659, tezacaftor and/or ivacaftor
  • Any acute lower respiratory symptoms treated with oral, inhaled or IV antibiotics or systemic corticosteroids within the 2 weeks prior to Visit 1.
  • Major or traumatic surgery within 12 weeks prior to Visit 1.
  • Initiation of any new chronic therapy (e.g., ibuprofen, Pulmozyme®, hypertonic saline, azithromycin, TOBI®, Cayston®) within 4 weeks prior to Visit 1.
  • Use of an investigational agent within 28 days prior to Visit 1.
  • History of lung or liver transplantation or listing for organ transplantation.

Key Trial Info

Start Date :

September 5 2019

Trial Type :

OBSERVATIONAL

Allocation :

ACTUAL

End Date :

February 26 2021

Estimated Enrollment :

8 Patients enrolled

Trial Details

Trial ID

NCT04038710

Start Date

September 5 2019

End Date

February 26 2021

Last Update

March 11 2021

Active Locations (1)

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1

National Jewish Health

Denver, Colorado, United States, 80206