Status:
ACTIVE_NOT_RECRUITING
Natural History Study of Patients With Canavan Disease (CANinform Study)
Lead Sponsor:
Aspa Therapeutics
Conditions:
Canavan Disease
Eligibility:
All Genders
Brief Summary
This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural histor...
Detailed Description
The CANinform natural history study is the first multinational effort to rigorously gather both retrospective and prospective data from this patient population. Data collection includes extraction of ...
Eligibility Criteria
Inclusion
- Meet age criteria of a specific cohort.
- Confirmed clinical and biochemical diagnosis of Canavan disease.
- Available medical records since birth that permit documentation of disease characteristics and developmental milestones.
- Parent and/or legal guardian is able to read, understand, and sign the informed consent.
Exclusion
- 1\. Patient does not meet the Inclusion Criteria.
Key Trial Info
Start Date :
October 10 2019
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
July 31 2025
Estimated Enrollment :
70 Patients enrolled
Trial Details
Trial ID
NCT04126005
Start Date
October 10 2019
End Date
July 31 2025
Last Update
June 22 2025
Active Locations (3)
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1
UCSF Benioff Children's Hospital Oakland
Oakland, California, United States, 94609
2
Massachusetts General Hospital
Boston, Massachusetts, United States, 02114
3
University Medical Center Hamburg-Eppendorf
Hamburg, Germany, 20246