Status:

UNKNOWN

Thalassemic Iron Overload Cardiomyopathy is Ameliorated by Taurine Supplementation

Lead Sponsor:

University Health Network, Toronto

Conditions:

Thalassemia Major

Eligibility:

All Genders

18+ years

Phase:

NA

Brief Summary

Hypothesis: Taurine, in combination with standard iron chelation therapy, is more effective than chelation therapy alone in reducing cardiac iron overload, oxidative stress and cardiac damage in β-Tha...

Eligibility Criteria

Inclusion

  • Participant inclusion criteria
  • Participants who meet all of the following criteria will qualify for entry into the study:
  • Diagnosis of transfusion-dependent Thalassemia being followed at the RBC clinic at TGH
  • Age 18 or older
  • On a stable dose of iron chelation for \>30 days. Combination iron chelation regimen is allowed in the study
  • Cardiac MRI T2\* ≥8ms measured within 3 months prior to randomization.
  • Preserved left ventricular ejection fraction (LVEF) \>50% as measured by cardiac MRI measured within 3 months prior to randomization.
  • Participant exclusion criteria
  • Participants who meet any of the following criteria will be excluded from the study:
  • More than 16 transfusions in the past 12 months or those who are anticipated to be on a 3 week transfusion schedule during the study period
  • Serum ferritin \< 500 ng/mL at screening
  • Liver iron concentration \> 40 mg/g dw as measured by liver R2 MRI (FerriScan) measured within 3 months prior to randomization
  • Signs and symptoms consistent with congestive heart failure in the opinion of the investigator
  • As a result of medical review, physical examination or screening investigations, the investigator considers the subject unfit for the study.
  • No fixed address
  • Interval advent of general contraindications to MRI.
  • Taking another investigational product within 30 days of anticipated date of randomization
  • Women who are currently pregnant or plan to become pregnant during the study period

Exclusion

    Key Trial Info

    Start Date :

    June 1 2020

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ESTIMATED

    End Date :

    October 31 2025

    Estimated Enrollment :

    60 Patients enrolled

    Trial Details

    Trial ID

    NCT04291352

    Start Date

    June 1 2020

    End Date

    October 31 2025

    Last Update

    October 3 2023

    Active Locations (1)

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    Page 1 of 1 (1 locations)

    1

    University Health Network

    Toronto, Ontario, Canada, M5G 2C4