Status:

TERMINATED

The Hemophilia Inhibitor Eradication Trial

Lead Sponsor:

Margaret Ragni

Collaborating Sponsors:

Health Resources and Services Administration (HRSA)

Conditions:

Hemophilia A With Inhibitor

Eligibility:

MALE

Phase:

PHASE3

Brief Summary

This is a multi-center randomized phase III clinical trial, the Inhibitor Eradication Trial, in which Eloctate ITI plus Emicizumab will be compared with Eloctate ITI alone to eradicate inhibitors in s...

Detailed Description

This is a multi-center randomized phase III clinical trial, the Inhibitor Eradication Trial, in which Eloctate ITI plus Emicizumab will be compared with Eloctate ITI alone to eradicate inhibitors in p...

Eligibility Criteria

Inclusion

  • Male adults or children \> 4 months of age.
  • Severe hemophilia A (FVIII \< 0.01 U/ml).
  • Current or past high-responding inhibitor, anti-FVIII \>= 5.0 B.U., ITI-refractory or ITI-naive.

Exclusion

  • Acquired hemophilia or any bleeding disorder other than hemophilia A.
  • Current use of Emicizumab, or if used, \> 8 weeks since last treatment.
  • Use of an experimental drug(s).
  • Surgery anticipated in the next 48 weeks.
  • Life expectancy less than 5 years.
  • Patient/parent/caretaker unable or unwilling to keep a personal diary of bleeding frequency and study drug treatment, make monthly visits and blood draws at weeks 4, 8, 12, 24, 36, and 48.
  • Other illness, condition, or reason in the opinion of the investigator that would make the patient unsuitable for the trial.

Key Trial Info

Start Date :

November 1 2021

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

June 27 2022

Estimated Enrollment :

1 Patients enrolled

Trial Details

Trial ID

NCT04303572

Start Date

November 1 2021

End Date

June 27 2022

Last Update

February 21 2023

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Hemophilia Center of Western PA

Pittsburgh, Pennsylvania, United States, 15213

2

University of Pittsburgh and Hemophilia Center Western PA

Pittsburgh, Pennsylvania, United States, 15213