Status:

COMPLETED

Evaluate the Efficacy and Safety of Rasburicase (Fasturtec®) in the Prevention and Treatment of Hyperuricemia in Pediatric Patients With Non-Hodgkin's Lymphoma and Acute Leukemia

Lead Sponsor:

Sanofi

Conditions:

Lymphoma

Eligibility:

All Genders

2-18 years

Phase:

PHASE4

Brief Summary

Primary Objective: To evaluate safety of rasburicase in pediatric patients with NHL and AL Secondary Objective: To assess efficacy of rasburicase for prevention and treatment of hyperuricemia

Detailed Description

Study duration per participants is approximatively 14 days including a 5-day treatment period.

Eligibility Criteria

Inclusion

  • Inclusion criteria :
  • Patient or parent/legal guardian is willing and able to provide signed informed consent, and if required, the patient is willing to provide assent.
  • Children or adolescent aged 2 to 18 years old (inclusive) at time of signing of informed consent.
  • At screening, the patient is expected to have a minimum life expectancy of 45 days and has a performance status (PS) no greater than 3 on the Eastern Cooperative Oncology Group (ECOG) scale, or a PS no less than 30 on the Lansky score as per the Investigator's preference (see Appendix D for ECOG and Lansky scale).
  • Newly diagnosed NHL or AL who is at the initiation of or during the first cycle of chemotherapy,baseline blood uric acid greater than 8 mg/dL (473 mol/L) at screening.
  • If newly diagnosed NHL patient with blood uric acid no greater than 8 mg/dL at screening, the patient must be diagnosed with Stage III or IV non-Hodgkin's lymphoma with high tumor burden which will be high risk of TLS defined, with one or more of following below: A. Burkitt lymphoma/leukemia or -lymphoblastic lymphoma, and/or B. Has at least one of lymph node or tumor, the diameter \>5 cm, and/or C. Lactate dehydrogenase (LDH) no less than 2 times the upper limit of normal (ULN).
  • If newly diagnosed AL patient is with blood uric acid no greater than 8 mg/dL at the screening but with a high risk of TLS defined with one of the following below criteria: A. White blood cell (WBC) no less than 100.0 10-9/L, or B. WBC \< 100.0 10-9/L with LDH no less than 2 ULN.
  • The patient will receive the chemotherapy, and will be confined in hospital for at least 14 days after first dose of rasburicase.
  • Exclusion criteria:
  • Acute promyelocytic leukemia
  • Patient who has been treated or planned to receive allopurinol within 72 hours of rasburicase administration.
  • Patients with abnormal liver or renal function: alanine aminotransferase (ALT) \>5 ULN, total bilirubin \>3 ULN, serum creatinine \>3 ULN.
  • Documented history of hereditary allergy or asthma.
  • Patients with known deficiency of glucose-6-phosphate dehydrogenase (G6PD), or a history of hemolytic disease or methemoglobinemia.
  • Patients with severe infection or active bleeding.
  • Previous therapy with urate oxidase.
  • Hypersensitive reaction against rasburicase or any of the other ingredients of the study drug.
  • Patient is not suitable for participation, whatever the reason, as judged by the Investigator, including medical or clinical conditions, or patients potentially at risk of noncompliance to study procedures.
  • Pregnant or breastfeeding woman.
  • Woman of childbearing potential (WOCBP) not protected by highly-effective method(s) of birth control and/or who are unwilling or unable to be tested for pregnancy (see contraceptive guidance in Appendix A).
  • Male participant with a female partner of childbearing potential not protected by highly-effective method(s) of birth control
  • The above information is not intended to contain all considerations relevant to a patient's potential participation in a clinical trial.

Exclusion

    Key Trial Info

    Start Date :

    May 14 2020

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ACTUAL

    End Date :

    March 12 2021

    Estimated Enrollment :

    50 Patients enrolled

    Trial Details

    Trial ID

    NCT04349306

    Start Date

    May 14 2020

    End Date

    March 12 2021

    Last Update

    April 25 2022

    Active Locations (1)

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    investigational site CHINA

    China, China