Status:

COMPLETED

To Evaluate the Safety, Tolerability and Pharmacokinetics of Oral NNZ-2591 in Healthy Volunteers

Lead Sponsor:

Neuren Pharmaceuticals Limited

Conditions:

Healthy Volunteers

Eligibility:

All Genders

18-55 years

Phase:

PHASE1

Brief Summary

The purpose of this study is to assess the safety, tolerability and pharmacokinetics of NNZ-2591 when administered to healthy volunteers.

Detailed Description

This study is in two stages: Stage 1: A First-in-Human (FIH), single dose escalation study of oral NNZ-2591 in healthy volunteers to establish safety, tolerability and pharmacokinetic parameters. St...

Eligibility Criteria

Inclusion

  • Male or female subjects aged 18 to 55 years, inclusive;
  • Weight at screening and admission between 45 kg and 100 kg;
  • Body mass index (BMI) between 18.0 and 32.0 kg/m2 inclusive;
  • Healthy as determined by the Investigator based on pre-study medical history, physical examination, vital signs, complete neurological examination and 12-lead electrocardiogram (ECG);
  • Negative tests for Hepatitis B surface antigen (HBsAg), hepatitis C virus antibody (anti-HCV) and human immunodeficiency virus (HIV)-1 and HIV-2 antibody at screening;
  • Clinical laboratory test results up to \>1.5 x Lower Limit of Normal (LLN) or \<1.5 x Upper Limit of Normal (ULN) at screening and admission and deemed not clinically significant by the Investigator;
  • Negative screen for alcohol and drugs of abuse at screening and admission;
  • Non-smokers or ex-smokers (must have ceased smoking \>3 months prior to screening visit);
  • If female:
  • Woman with no childbearing potential by reason of surgery or at least 1year post- menopause (i.e., 12 months post last menstrual period), and menopause confirmed by follicle-stimulating hormone (FSH) testing;
  • If of childbearing potential, using an effective nonhormonal method of contraception (intrauterine device; condom or occlusive cap \[diaphragm or cervical or vault caps\]; true abstinence; or vasectomized male partner (provided that he is the sole partner of that subject and had a vasectomy ≥30 days prior to screening) for the duration of the study and up to one month after the last investigational medicinal product (IMP) administration;
  • Negative serum pregnancy test at screening and negative urine pregnancy test on admission (women of childbearing potential only);
  • If male:
  • Using an effective method of contraception (condom) if sexually active with a female partner of child-bearing potential; true abstinence; or vasectomy ≥30 days prior to screening) throughout the study and for one month after the last IMP administration.

Exclusion

  • Subjects who have a clinically relevant history as determined by the Investigator, or presence of respiratory, gastrointestinal, renal, hepatic, haematological, lymphatic, neurological, cardiovascular, psychiatric, musculoskeletal, genitourinary, immunological, dermatological, endocrine, connective tissue diseases or disorders;
  • Fridericia's correction factor for QT (QTcF) \> 450 ms for male participants and \>470ms for female participants or history of QT interval prolongation.
  • Have a clinically relevant surgical history, as determined by the Investigator;
  • Have a history of relevant atopy or drug hypersensitivity;
  • Have a history of alcoholism or drug abuse;
  • Consume more than 21 standard drinks a week for males and more than 14 standard drink if female \[1 standard drink is any drink containing 10g of alcohol, regardless of container size or alcohol type\].
  • Have a significant infection or known inflammatory process on screening or admission;
  • Have acute gastrointestinal symptoms (e.g., nausea, vomiting, diarrhea, heartburn) at the time of screening or admission;
  • Have used any prescription or non-prescription medicines within 2 weeks of admission, unless in the investigator's opinion will not affect determination of safety or other study assessments. Occasional paracetamol use (up to 2g/day is permitted);
  • Have received any investigational drug within 30 days prior to screening;
  • Have used tobacco or nicotine products within 3 months of screening
  • Have donated or received any blood or blood products within the 3 months prior to screening;
  • Cannot communicate reliably with the investigator;
  • Are unlikely to co-operate with the requirements of the study;
  • Are unwilling or unable to give written informed consent.
  • If female:
  • Pregnancy or breast-feeding;
  • Woman of childbearing potential not willing to use an accepted effective contraceptive method or using hormonal contraceptives;
  • If male:
  • Not willing to use an accepted effective method of contraception.

Key Trial Info

Start Date :

May 29 2020

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 11 2021

Estimated Enrollment :

28 Patients enrolled

Trial Details

Trial ID

NCT04379869

Start Date

May 29 2020

End Date

February 11 2021

Last Update

July 9 2021

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Scientia Clinical Research

Sydney, New South Wales, Australia, 2031

2

Linear Clinical Research, The Queen Elizabeth II Medical Centre

Nedlands, Western Australia, Australia, 6009