Status:

UNKNOWN

NIPD on cffDNA for Triplet Repeat Diseases

Lead Sponsor:

University Hospital, Montpellier

Collaborating Sponsors:

Agence de La Biomédecine

Conditions:

Myotonic Dystrophy 1

Huntington Disease

Eligibility:

All Genders

18+ years

Brief Summary

The purprose of this study is to develop and validate an analytical NIPD test for triplet repeat disesases by NGS analysis from maternal blood, searching for the familial mutation in families at risk ...

Detailed Description

Context: The ability to sequence fetal cfDNA has led to exciting new developments for the non-invasive genetic diagnosis of monogenic diseases (DPNI\_MGR). Various tests are proposed for diseases wit...

Eligibility Criteria

Inclusion

  • Inclusion criteria:
  • Couple at risk (based on family history or echographic findings) for one of the following diseases: Huntington's disease, Steinert's myotonic dystrophy, fragile X
  • Written informed consent was obtained for DIACCIMEX study and mentionned "authorization for use for further studies on familial pathology. Indeed, the DNA can be used anonymized for the development of new analyzes of non-invasive prenatal diagnosis".
  • Prenatal diagnosis has been done for the pregnancy during which maternal blood has been collected
  • Couple molecular diagnosis results for one of the following diseases (Huntington's disease, Steinert's myotonic dystrophy, fragile X and spinocerebellar ataxias 1, 2 or 3 ) MUST BE AVAILABLE.
  • Exclusion criteria:
  • Couple Genomic DNA are unavailable
  • Subjects at risk of transmitting the family disease, but not wishing to know their molecular status
  • Individuals under guardianship by court order

Exclusion

    Key Trial Info

    Start Date :

    September 1 2020

    Trial Type :

    OBSERVATIONAL

    Allocation :

    ESTIMATED

    End Date :

    December 1 2023

    Estimated Enrollment :

    36 Patients enrolled

    Trial Details

    Trial ID

    NCT04698551

    Start Date

    September 1 2020

    End Date

    December 1 2023

    Last Update

    January 7 2021

    Active Locations (1)

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    Page 1 of 1 (1 locations)

    1

    CHU Montpellier

    Montpellier, France, 34295