Status:

UNKNOWN

Prevalence of Adenosine Deaminase (ADA) Enzyme Deficiency Disease in Adult Patients With Pulmonary Alveolar Proteinosis

Lead Sponsor:

TRPHARM

Conditions:

Pulmonary Alveolar Proteinosis

Eligibility:

All Genders

18-70 years

Brief Summary

This observational study was designed as a prospective epidemiological screening study. Patients who have applied to the centers participating in the study and who have previously been clinically or p...

Detailed Description

PAP (Pulmonary alveolar proteinosis) is a rare disease with a frequency of 0.36 per million. As a result of intensive accumulation of surfactant components in the lungs, it leads to respiratory distre...

Eligibility Criteria

Inclusion

  • Signing of the written informed consent form by the patient and/or his legal representative,
  • The patient should be between the ages of 18 and 70,
  • Diagnosis of PAP: The patient has been diagnosed with PAP clinically or histologically.

Exclusion

  • The patient was diagnosed with ADA enzyme deficiency before being included in the study,
  • The patient's PAP diagnosis is secondary to an occupational disease such as silicosis,
  • The patient's PAP diagnosis is secondary to an oncological disease,
  • The patient has participated in an interventional clinical trial within the last 30 days,
  • The patient himself and/or his legal representative did not give their consent to participate in the study,
  • According to the researcher's opinion, the patient will not be able to properly fulfill the study requirements,
  • \* Pregnancy and/or lactation period,
  • The fact that the volunteer participating in the study received an erythrocyte suspension or a complete blood transfusion within the last 3 months.

Key Trial Info

Start Date :

August 16 2021

Trial Type :

OBSERVATIONAL

Allocation :

ESTIMATED

End Date :

August 16 2022

Estimated Enrollment :

15 Patients enrolled

Trial Details

Trial ID

NCT05300360

Start Date

August 16 2021

End Date

August 16 2022

Last Update

March 29 2022

Active Locations (1)

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Istanbul Yedikule Chest Diseases and Thoracic Surgery Training and Research Hospital

Istanbul, Maltepe, Turkey (Türkiye)