Status:

ENROLLING_BY_INVITATION

Evaluating Long-term Safety of Efgartigimod Administered Intravenously and Efgartigimod PH20 Administered Subcutaneously in Children With Generalized Myasthenia Gravis

Lead Sponsor:

argenx

Conditions:

Generalized Myasthenia Gravis

gMG

Eligibility:

All Genders

2-18 years

Phase:

PHASE2

PHASE3

Brief Summary

The purpose of this trial is to evaluate the long-term safety of efgartigimod IV and efgartigimod PH20 SC administered to participants with gMG in the antecedent studies, ARGX-113-2006 and ARGX-113-22...

Eligibility Criteria

Inclusion

  • The participant completed ARGX-113-2006, defined as:
  • The participant reached End of Trial in trial ARGX-113-2006 or End of Study in ARGX-113-2207 and agreed to participate in the ARGX-113-2008 trial.
  • The participant qualifies for retreatment in trial ARGX-113-2006, but cannot complete a Treatment Period (TP) and the required Intertreatment Period (IP) visits within the ARGX-113-2006 trial's timeframe.
  • Either the participant or the participant's legally authorized representative can understand the requirements of the trial and provide written informed consent/assent, and willingness and ability to comply with the trial protocol procedures.
  • Contraceptive use for sexually active participants should be consistent with local regulations for those participating in clinical studies.

Exclusion

  • Female adolescents of childbearing potential (FAOCBP): Pregnancy or lactation, or the participant intends to become pregnant during their participation in the study.
  • Discontinued early from ARGX-113-2006 or ARGX-113-2207 treatment.
  • Clinically significant uncontrolled chronic bacterial, viral, or fungal infection at study entry not sufficiently resolved in the investigator's opinion or known autoimmune disease or any medical condition that would interfere with an accurate assessment of clinical symptoms of gMG or put the participant at undue risk.

Key Trial Info

Start Date :

August 18 2022

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

September 1 2029

Estimated Enrollment :

12 Patients enrolled

Trial Details

Trial ID

NCT05374590

Start Date

August 18 2022

End Date

September 1 2029

Last Update

December 16 2025

Active Locations (15)

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Page 1 of 4 (15 locations)

1

Ann and Robert H Lurie Children's Hospital of Chicago - Main Hospital

Chicago, Illinois, United States, 60611

2

University of Virginia (UVA) Health - Developmental Pediatrics Clinic

Charlottesville, Virginia, United States, 22903

3

Universitair Ziekenhuis Antwerpen

Edegem, Belgium, 2650

4

UZ Gent

Ghent, Belgium, 9000