Status:

COMPLETED

Proof of Concept Study to Assess the Efficacy, Safety of HRS-5965 in Patients With Paroxysmal Nocturnal Hemoglobinuria

Lead Sponsor:

Chengdu Suncadia Medicine Co., Ltd.

Conditions:

Paroxysmal Nocturnal Hemoglobinuria

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This is a multicenter, randomized, open-label phase II clinical trial. A total of 24 patients with paroxysmal nocturnal hemoglobinuria naïve to complement inhibitor therapy were included. Subjects wer...

Eligibility Criteria

Inclusion

  • Diagnosis of PNH confirmed by flow cytometry with clone size ≥ 10%.
  • Have not received complement inhibitor therapy ;
  • LDH \> 1.5×ULN;
  • Hemoglobin level \< 10 g/dL.

Exclusion

  • Known or suspected hereditary or acquired complement deficiency;
  • Patients with laboratory evidence of bone marrow failure (reticulocytes \<100x109/L; platelets \<30x109/L; neutrophils \<0.5x109/L);
  • Presence or suspicion of a systemic active bacterial, viral, or fungal infection (based on judgment of the investigator) within 2 weeks prior to the first dose of HRS-5965;
  • History of infection with capsular bacteria (e.g., meningococcus, pneumococcus, etc.)
  • Positive of HIV, HBsAg or HCVAb.

Key Trial Info

Start Date :

November 15 2023

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

March 25 2024

Estimated Enrollment :

26 Patients enrolled

Trial Details

Trial ID

NCT06051357

Start Date

November 15 2023

End Date

March 25 2024

Last Update

October 15 2024

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Peking Union Medical College Hospital, Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, China, 100730

2

The Blood Disease Hospital of the Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China, 300020