Status:

COMPLETED

Acceptability of Expanded Newborn Screening to Parents in France With or Without Genetics in the First Line

Lead Sponsor:

Centre Hospitalier Universitaire Dijon

Conditions:

Expanded Newborn Screening

Parental Acceptability

Eligibility:

All Genders

18-60 years

Brief Summary

The recent modifications of the French bioethics law, the therapeutic progress and the massive development of advanced genetic techniques (such Next-Generation Sequencing (NGS)) with a rapid decrease ...

Eligibility Criteria

Inclusion

  • All populations combined:
  • Be a parent or co-parent
  • Age of parent:
  • woman between 18 and 50 years
  • man between 18 and 60 years
  • Live in metropolitan France
  • Have received information about the SeDeN-p3 Study
  • Understand the purpose of the SeDeN-p3 Study
  • Self-administered questionnaire:
  • Be able to read and answer a self-administered questionnaire in French
  • Population 1Q:
  • Have a child less than a week old
  • Have just giver birth in 1 of the partner maternity hospitals during the survey period
  • Population 2:
  • Parent or co-parent whose youngest child is between 1 week and 3 years old
  • Be part of the panel of the selected survey-sample firm
  • Semi-structured interviews
  • Can converse fluently in French
  • Accept to conduct a recorded interview
  • Population 1E (sub-population of Population 1Q)
  • Have completed the entire questionnaire
  • Population 3
  • Have a child under 5 years old (inclusive) with 1 of the following diseases :
  • Phenylketonuria
  • Congenital hypothyroidism
  • Congenital adrenal hyperplasia
  • Cystic fibrosis
  • Sickle cell disease
  • hearing loss
  • MCAD deficiency
  • glutaric aciduria type -1
  • isovaleric academia
  • LCHAD deficiency
  • carnitine deficiency
  • homocystinuria
  • leukinosis
  • tyrosinemia type 1
  • Population 4
  • Have a child under 17 years old (inclusive), with 1 of following diseases:
  • Citrullinemia type I
  • Ornithine Transcarbamylase Deficiency
  • Methylmalonic acidaemia
  • Very long-chain acyl-CoA dehydrogenase deficiency
  • Carnitine palmitoyl transferase 1 deficiency
  • Carnitine palmitoyl transferase 2 deficiency
  • Glutaric acidaemia type II
  • Galactosaemia
  • Biotinidase deficiency
  • Pompe Disease
  • Mucopolysaccharidosis Type 1
  • Glucose-6-phophate dehydrogenase deficiency
  • X-linked Adrenoleukodystrophy
  • Spinal muscular atrophy linked to SMN1
  • S, beta-thalassemia

Exclusion

  • Have a newborn child die during the recruitment period
  • Not speak and/or understand French
  • Refuse to participate in the SeDeN-p3 Study
  • Be under judicial protection (tutelle, curatelle, habilitation familiale et sauvegarde de justice)

Key Trial Info

Start Date :

September 1 2022

Trial Type :

OBSERVATIONAL

Allocation :

ACTUAL

End Date :

June 1 2023

Estimated Enrollment :

1585 Patients enrolled

Trial Details

Trial ID

NCT06111456

Start Date

September 1 2022

End Date

June 1 2023

Last Update

November 1 2023

Active Locations (4)

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Page 1 of 1 (4 locations)

1

Hopital Antoine Beclere - Aphp

Clamart, France, 92140

2

Chu Dijon Bourgogne

Dijon, France, 21000

3

Hôpital Necker - Enfants Malades

Paris, France, 75015

4

Groupe Hospitalier de La Haute-Saône

Vesoul, France, 70000