Status:

RECRUITING

A Safety Assessment of Oral Letermovir in Infants With Symptomatic Congenital Cytomegalovirus

Lead Sponsor:

National Institute of Allergy and Infectious Diseases (NIAID)

Conditions:

Congenital Cytomegalovirus Infection

Eligibility:

All Genders

Up to 90 years

Phase:

PHASE1

Brief Summary

This is a Phase 1 single-arm open-label study of letermovir in neonates with symptomatic congenital Cytomegalovirus (CMV) disease. There will be two groups enrolled. Group 1 will be comprised of 4 sub...

Detailed Description

This is a Phase 1 single-arm open-label study of letermovir in neonates with symptomatic congenital Cytomegalovirus (CMV) disease. There will be two groups enrolled. Group 1 will be comprised of 4 sub...

Eligibility Criteria

Inclusion

  • Signed informed consent from parent(s) or legal guardian(s)
  • Cytomegalovirus (CMV) confirmation by culture, shell vial, or Polymerase Chain Reaction (PCR) tests from a specimen obtained at \</= 30 days of life from saliva, blood, or urine
  • Symptomatic congenital CMV disease\*
  • Age at study enrollment:
  • \</= 83 days for Group 1 subjects\*\*
  • \</= 90 days for Group 2 subjects
  • Weight at study enrollment 2.6 kg to \< 8.0 kg
  • Gestational age \>/= 32 weeks at birth
  • Intention by patient's physician to clinically treat infant with oral valganciclovir for 6 months for symptomatic congenital CMV disease
  • Manifested by one or more of the following: thrombocytopenia; petechiae; hepatomegaly; splenomegaly; intrauterine growth restriction; hepatitis; or Central Nervous System (CNS) involvement such as microcephaly, radiographic abnormalities indicative of CMV CNS disease, abnormal cerebrospinal fluid (CSF) indices for age, chorioretinitis, hearing deficits as detected by formal brainstem evoked response, and/or positive CMV Polymerase Chain Reaction (PCR) from CSF \*\*Group 1 subjects must enroll and receive the Dose Finding Day dose of letermovir on or before 83 days of life so that oral valganciclovir can be started prior to 12 weeks 6 days (which is 90 days) of life, as is standard of care. For this study, the date of birth is counted as day of life 0

Exclusion

  • Imminent demise
  • Infants known to be born to women who are HIV positive (but HIV testing is not required for study entry)
  • Current receipt of other investigational drugs
  • Grade 3 or 4 alanine aminotransferase (ALT) utilizing Division of AIDS (DAIDS) Toxicity Table
  • Grade 3 or 4 total bilirubin utilizing DAIDS Toxicity Table
  • Gastrointestinal abnormality which might preclude absorption of an oral medication (e.g., a history of necrotizing enterocolitis)
  • Anticipated concomitant administration of carbamazepine (Tegretol), nafcillin, phenobarbital, or phenytoin (Dilantin) during the period of study drug administration

Key Trial Info

Start Date :

February 19 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

August 31 2026

Estimated Enrollment :

12 Patients enrolled

Trial Details

Trial ID

NCT06118515

Start Date

February 19 2025

End Date

August 31 2026

Last Update

January 5 2026

Active Locations (10)

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Page 1 of 3 (10 locations)

1

Children's of Alabama Child Health Research Unit (CHRU)

Birmingham, Alabama, United States, 35233-0011

2

Children's National Medical Center - Sheikh Zayed Campus - Infectious Disease

Washington D.C., District of Columbia, United States, 20010-2916

3

Emory University School of Medicine

Atlanta, Georgia, United States, 30322-1014

4

University of Louisville School of Medicine - Norton Children's Hospital - Infectious Diseases

Louisville, Kentucky, United States, 40202