Status:
RECRUITING
VIrtual STudy in Achondroplasia for the US (VISTA)
Lead Sponsor:
BioMarin Pharmaceutical
Collaborating Sponsors:
PicnicHealth
Conditions:
Achondroplasia
Eligibility:
All Genders
Up to 18 years
Brief Summary
This is an observational study of individuals with achondroplasia in the United States. The primary study population consists of pediatric individuals treated and untreated with VOXZOGO™. Study enroll...
Eligibility Criteria
Inclusion
- Physician diagnosis of achondroplasia
- Age at time of enrollment:
- Primary Pediatric Cohort: ≤13 years old Secondary Adolescent and Adult Cohort: ≥14 years old
- Receiving medical care in the United States
- Complete PicnicHealth's onboarding process, including signing informed consent and authorization for medical record retrieval
Exclusion
- Lack of any medical records
Key Trial Info
Start Date :
February 21 2023
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
February 1 2028
Estimated Enrollment :
170 Patients enrolled
Trial Details
Trial ID
NCT06168201
Start Date
February 21 2023
End Date
February 1 2028
Last Update
December 18 2025
Active Locations (7)
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1
UCSF
Oakland, California, United States, 94609
2
PicnicHealth
San Francisco, California, United States, 94107
3
Piedmont Health
Statesville, North Carolina, United States, 28625
4
University of Cincinnati
Cincinnati, Ohio, United States, 45229