Status:
NOT_YET_RECRUITING
Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy
Lead Sponsor:
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Conditions:
Duchenne Muscular Dystrophy
Eligibility:
MALE
Brief Summary
Duchenne muscular dystrophy is a rare progressive X-linked neuromuscular disease, caused by mutation in the dystrophin gene, leading to progressive muscle degeneration, loss of specific functional mil...
Detailed Description
Duchenne muscular Dystrophy is a progressive disorder affecting one in 3600-5000 live male births, leading to a progressive loss of specific functional milestones. Over the past two decades, the deve...
Eligibility Criteria
Inclusion
- patient with genetic confirmation od Duchenne Muscular Dystrophy in follow up in one of the 4 involved centers
- signed informed consent form
Exclusion
- patients who refuses consent
Key Trial Info
Start Date :
November 1 2024
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
November 1 2026
Estimated Enrollment :
200 Patients enrolled
Trial Details
Trial ID
NCT06579859
Start Date
November 1 2024
End Date
November 1 2026
Last Update
August 30 2024
Active Locations (4)
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1
ASL LANCIANO VASTO CHIETI, Laboratorio di Patologie Neuromuscolari del Centro di Riferimento Regionale per le Malattie Neuromuscolari
Chieti, Ch, Italy, 66100
2
ASST Grande Ospedale Metropolitano Niguarda, Centro Clinico Nemo Milano
Milan, MI, Italy, 20162
3
Azienda Ospedaliera Universitaria "G. Martino"UOC di Neurologia e Malattie Neuromuscolari
Messina, Italy, 98125
4
Fondazione Policlinico Universitario A. Gemelli IRCCS, UOC NEMO Pediatrico
Roma, Italy, 00168