Status:

NOT_YET_RECRUITING

Proof-of-Concept Study of ACT001 in Adult Patients With Recurrent Glioblastoma Harbouring STAT3-High Signature

Lead Sponsor:

National Neuroscience Institute

Conditions:

Recurrent Glioblastoma

Eligibility:

All Genders

21+ years

Phase:

PHASE2

Brief Summary

This trial will study the effectiveness of ACT001 in adult patients whose Glioblastoma have recurred with a STAT3-high signature after standard-of-care treatment with at least radiation therapy.

Eligibility Criteria

Inclusion

  • Histologically confirmed diagnosis of GBM according to 2021 WHO classification
  • Availability of tumor tissue representative of GBM from definitive surgery or biopsy and tested to harbour STAT3-High Signature
  • Previous treatment with at least radiation therapy
  • Documented recurrence of malignant glioma by diagnostic biopsy, resection or MRI performed within 21 days of study enrolment per RANO criteria.
  • There is no limit on number of previous recurrences or lines of treatment
  • At least 12 weeks after the end of prior radiation therapy is required unless there is either: i) histopathologic confirmation of recurrent tumor, or ii) n new enhancement on MRI outside of the radiation treatment field
  • An interval of at least 4 weeks after the last administration of any investigational agent or any other treatment prior to first dose of STAT3 inhibitor
  • Age 21 years or older on the day of signing informed consent
  • Karnofsky performance status (KPS) of 70 or higher
  • Patient has adequate bone marrow, renal, and hepatic function ≤ 21 days prior to study enrolment (Step 2) as follows:
  • Absolute neutrophil count (ANC) ≥1,500/mm3
  • Platelets ≥ 100,000/mm3
  • Hemoglobin (Hgb) ≥ 9.0 g/dL (Note: The use of transfusion or other intervention to achieve Hgb ≥ 9.0 g/dL is acceptable.)
  • Renal function: calculated creatinine clearance ≥ 30 mL/min by the Cockcroft-Gault formula
  • Hepatic function: Total bilirubin, Aspartate Aminotransferase (AST), and Alanine Aminotransferase (ALT) ≤ 1.5 times upper limit of normal (ULN). Patients with Gilbert's syndrome documented in medical history may be enrolled if bilirubin is \< 3 times ULN.

Exclusion

  • Presence of extracranial metastatic or leptomeningeal disease
  • Previous or current treatment with a JAK or STAT3 inhibitor
  • Previous or current treatment with bevacizumab/VEGF inhibitor
  • Patient is a lactating or pregnant female.
  • Symptomatic intra-tumoural haemorrhage
  • Severe, active co-morbidity, defined as follows:
  • Patients with clinically defined Acquired Immune-Deficiency Syndrome (AIDS)-defining illness.
  • Active connective tissue disorders, such as lupus or scleroderma, that in the opinion of the Investigator may put the patient at high risk of toxicity
  • Any other major medical illnesses or psychiatric impairments that in the Investigator's opinion will prevent administration or completion of protocol therapy

Key Trial Info

Start Date :

April 1 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

May 1 2026

Estimated Enrollment :

12 Patients enrolled

Trial Details

Trial ID

NCT06894225

Start Date

April 1 2025

End Date

May 1 2026

Last Update

April 6 2025

Active Locations (1)

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National Neuroscience Institute

Singapore, Singapore

Proof-of-Concept Study of ACT001 in Adult Patients With Recurrent Glioblastoma Harbouring STAT3-High Signature | DecenTrialz