Status:

RECRUITING

Efficacy, Safety, and Pharmacokinetics of LP-005 Injection in PNH Patients.

Lead Sponsor:

Longbio Pharma

Conditions:

PNH - Paroxysmal Nocturnal Hemoglobinuria

Eligibility:

All Genders

18-65 years

Phase:

PHASE2

Brief Summary

This is a multicenter, randomized, open-label, Phase II clinical study to evaluate the efficacy, safety, and pharmacokinetics of LP-005 injection in adult patients with paroxysmal nocturnal hemoglobin...

Eligibility Criteria

Inclusion

  • Male or female, aged 18 to 65 years.
  • Diagnosis of PNH based on flow cytometry with clone size \> 10% by granulocytes.
  • Presence of one or more PNH-related signs or symptoms within 3 months prior to screening or a history of transfusion due to PNH.
  • LDH level ≥2.0×upper limit of the normal range(ULN).
  • Hemoglobin level \<100 g/L at screening.

Exclusion

  • Active or suspected active viral, bacterial, fungal, or parasitic infection within 14 days prior to screening.
  • History of meningococcal infection.
  • History of splenectomy or congenital asplenia.
  • History of systemic autoimmune disease or known/suspected immunodeficiency.
  • History of hematopoietic stem cell transplantation.
  • Use of any complement inhibitor within 3 months prior to screening or within 5 drug half-lives (whichever is longer).
  • Pregnant or breastfeeding women, or women planning to become pregnant during the study or follow-up period.

Key Trial Info

Start Date :

November 14 2024

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

March 31 2028

Estimated Enrollment :

30 Patients enrolled

Trial Details

Trial ID

NCT07212426

Start Date

November 14 2024

End Date

March 31 2028

Last Update

October 8 2025

Active Locations (1)

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1

The First Affiliated Hospital of Nanjing Medical University

Nanjing, China