Status:

NOT_YET_RECRUITING

Comprehensive Program for Hereditary Transthyretin Amyloidosis

Lead Sponsor:

Hospital de Alta Complejidad en Red

Conditions:

Amyloidosis in Transthyretin (TTR)

Amyloidosis, Familial

Eligibility:

All Genders

18+ years

Brief Summary

The Comprehensive Program for Hereditary Transthyretin Amyloidosis describes a prospective observational study focused on understanding hereditary transthyretin amyloidosis (ATTR), a progressive and p...

Eligibility Criteria

Inclusion

  • Participants with a pathogenic variant of the TTR gene (Hereditary Amyloidosis)

Exclusion

  • wild-type TTR amyloidosis

Key Trial Info

Start Date :

October 1 2025

Trial Type :

OBSERVATIONAL

Allocation :

ESTIMATED

End Date :

December 1 2028

Estimated Enrollment :

20 Patients enrolled

Trial Details

Trial ID

NCT07213297

Start Date

October 1 2025

End Date

December 1 2028

Last Update

October 8 2025

Active Locations (1)

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Page 1 of 1 (1 locations)

1

Hospital Cuenca Alta de Cañuelas

Cañuelas, Buenos Aires, Argentina, 1814