Status:

RECRUITING

Trial of Orca-T Following Reduced Intensity or Nonmyeloablative Conditioning in Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome

Lead Sponsor:

Orca Biosystems, Inc.

Conditions:

Leukemia, Myeloid, Acute

Myelodysplastic Syndromes

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This study will evaluate the safety, tolerability, and efficacy of Orca-T in participants undergoing reduced intensity or non-myeloablative allogeneic hematopoietic cell transplantation (alloHCT) for ...

Detailed Description

This study is a multicenter, open-label phase 2 trial of Orca-T in adults with acute myeloid leukemia or myelodysplastic syndrome who are not able to receive myeloablative (high intensity) conditionin...

Eligibility Criteria

Inclusion

  • Age ≥18 years at the time of enrollment
  • Diagnosed with 1 of the following diseases:
  • Acute myeloid, or mixed phenotype leukemia in complete remission (CR) or CR with incomplete hematologic recovery (CRi), with or without the presence of known minimal residual disease.
  • Myelodysplastic syndrome that is indicated for alloHCT per the 2017 International Expert Panel recommendations and/or therapy-related/secondary MDS as defined by the World Health Organization (WHO) classification of myeloid malignancies, with ≤10% blast burden in the bone marrow.
  • Planned to undergo 1 of the following preparative regimens as per Investigator discretion:
  • RIC cohort: Planned RIC-alloHCT including RIC regimen with TBI/thiotepa/fludarabine
  • NMA cohort: Planned NMA-alloHCT including NMA regimen with fludarabine/cyclophosphamide/TBI
  • Identified related or unrelated donor who is an 8/8 match for HLA-A, -B, -C, and -DRB1
  • Estimated glomerular filtration rate ≥30 mL/minute
  • Cardiac ejection fraction at rest ≥40% or shortening fraction of ≥22% by echocardiogram or radionuclide scan (MUGA)
  • Diffusing capacity of the lung for carbon monoxide (adjusted for hemoglobin) ≥40%
  • Negative serum or urine β-HCG test in persons of childbearing potential
  • Alanine transaminase (ALT)/aspartate transaminase (AST) \<5 times the upper limit of normal (ULN)
  • Total bilirubin \<3 × ULN
  • Deemed ineligible for a fully myeloablative alloHCT per assessment of the principal investigator

Exclusion

  • Prior alloHCT
  • Currently receiving corticosteroids or other immunosuppressive therapy. Topical corticosteroids or oral systemic corticosteroid doses less than or equal to 10 mg/day are allowed.
  • Planned donor lymphocyte infusion (DLI)
  • Planned pharmaceutical in vivo or ex vivo T-cell depletion
  • Recipient-positive antidonor HLA antibodies against a mismatched allele in the selected donor
  • Karnofsky performance score \<60%
  • For RIC cohort only: HCT-Specific Comorbidity Index (HCT-CI) ≥6
  • Uncontrolled bacterial, viral, or fungal infection (currently taking antimicrobial therapy and with progression or no clinical improvement) at the time of enrollment
  • Seropositive for HIV-1 or -2, HTLV-1 or -2, hepatitis B surface antigen, or HCV antibody unless previously treated with curative therapy and are HCV NAT negative
  • Known allergy or hypersensitivity to or intolerance of tacrolimus
  • Documented allergy or hypersensitivity to iron dextran or bovine, murine, algal, or Streptomyces avidinii proteins
  • Any uncontrolled autoimmune disease requiring active immunosuppressive treatment
  • Concurrent malignancy within 1 year except nonmelanoma skin cancer that has been curatively resected
  • Psychosocial circumstances that preclude the participant being able to go through transplantation or participate responsibly in follow-up care
  • Persons who are pregnant or breastfeeding
  • Person of childbearing potential (POCBP) or men who have sexual contact with POCBP who are unwilling to use effective forms of birth control or abstinence for 1 year after transplantation.
  • Any serious medical condition or abnormality in clinical laboratory tests that, in the investigator's or medical monitor's judgment, precludes the recipient's safe participation in and completion of the trial or which could affect compliance with the protocol or interpretation of results

Key Trial Info

Start Date :

December 9 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

December 1 2028

Estimated Enrollment :

80 Patients enrolled

Trial Details

Trial ID

NCT07216443

Start Date

December 9 2025

End Date

December 1 2028

Last Update

January 8 2026

Active Locations (4)

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Page 1 of 1 (4 locations)

1

UCLA Department of Medicine

Los Angeles, California, United States, 90095

2

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States, 07601

3

Oregon Health and Science University

Portland, Oregon, United States, 97239

4

Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37221